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Elevation of plasma lysosphingomyelin-509 and urinary bile acid metabolite in Niemann-Pick disease type C-affected individuals - Top Articles selected by the Editor - Molecular Genetics and Metabolism Reports - Journal - Elsevier
![NNPDF on Twitter: "October is Global Niemann-Pick Disease Awareness Month! For more information on Niemann-Pick Disease or to make a donation to NNPDF go to https://t.co/zWwdlaFmx3. #niemannpick #ASMD #NPC #raredisease #NNPDF #NiemannPickC NNPDF on Twitter: "October is Global Niemann-Pick Disease Awareness Month! For more information on Niemann-Pick Disease or to make a donation to NNPDF go to https://t.co/zWwdlaFmx3. #niemannpick #ASMD #NPC #raredisease #NNPDF #NiemannPickC](https://pbs.twimg.com/media/Dpo0LXuU8AARxgn.jpg)
NNPDF on Twitter: "October is Global Niemann-Pick Disease Awareness Month! For more information on Niemann-Pick Disease or to make a donation to NNPDF go to https://t.co/zWwdlaFmx3. #niemannpick #ASMD #NPC #raredisease #NNPDF #NiemannPickC
![Niemann-Pick disease type C. The diagram represents subtypes and onset... | Download Scientific Diagram Niemann-Pick disease type C. The diagram represents subtypes and onset... | Download Scientific Diagram](https://www.researchgate.net/publication/325129323/figure/fig1/AS:626243703676928@1526319542361/Niemann-Pick-disease-type-C-The-diagram-represents-subtypes-and-onset-ages-of-visceral.png)
Niemann-Pick disease type C. The diagram represents subtypes and onset... | Download Scientific Diagram
![Frontiers | Adult-Onset Niemann–Pick Disease Type C: Rapid Treatment Initiation Advised but Early Diagnosis Remains Difficult Frontiers | Adult-Onset Niemann–Pick Disease Type C: Rapid Treatment Initiation Advised but Early Diagnosis Remains Difficult](https://www.frontiersin.org/files/MyHome%20Article%20Library/237917/237917_Thumb_400.jpg)
Frontiers | Adult-Onset Niemann–Pick Disease Type C: Rapid Treatment Initiation Advised but Early Diagnosis Remains Difficult
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